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Sangamo Therapeutics Inc是一家臨床階段的基因組醫學公司。該公司專注於利用其優化的鋅指(ZF)技術,一種用於開發基因組藥物的差異化工具,包括同種異體細胞療法和體內基因組工程療法。其候選產品包括Isaralgagene civaparvovec,也稱為ST-920,是其自有的基因治療候選產品,用於治療法布里病;SAR445136,ZF核酸酶,是一種基因編輯細胞治療候選產品,用於治療鐮狀細胞病(SCD);TX200,是其自有的嵌合抗原受體(CAR)工程調節性T細胞(CAR-Treg),該細胞治療候選產品用於預防HLA-A2錯配腎移植中免疫介導排斥;Giroctocogene fitelparvovec,也稱為SB-525,是一種用於治療中度至重度血友病A的基因治療候選產品。
名稱 | 年齡 | 成立於 | 主旨 |
---|---|---|---|
H. Stewart Parker | 68 | 2014 | Independent Chairwoman of the Board |
Jef D. Boeke | - | 2019 | Member of Scientific Advisory Board |
Robert F. Carey | 65 | 2016 | Independent Director |
Karen L. Smith | 56 | 2018 | Independent Director |
Megan Levings | - | 2019 | Member of Scientific Advisory Board |
Stuart L. Schreiber | 68 | 2019 | Member of Scientific Advisory Board |
Courtney Beers | 54 | 2022 | Independent Director |
Kenneth J. Hillan | 63 | 2020 | Independent Director |
James R. Meyers | 59 | 2019 | Independent Director |
Samuel A. J. R. Aparicio | - | 2019 | Member of Scientific Advisory Board |
Douglas Higgs | - | 2019 | Member of Scientific Advisory Board |
Alexander D. Macrae | 61 | 2016 | CEO, President & Director |
John H. Markels | 58 | 2020 | Independent Director |
Steven W. Pipe | - | 2019 | Member of Scientific Advisory Board |
J. Fraser Wright | - | 2019 | Member of Scientific Advisory Board |
Michael Grunstein | - | 2019 | Member of Scientific Advisory Board |
Robert J. Desnick | - | 2019 | Member of Scientific Advisory Board |
Roger D. Kornberg | 77 | 2019 | Member of Scientific Advisory Board |
Margaret A. Horn | 61 | 2022 | Independent Director |
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